Cystic fibrosis: Triple therapy is particularly effective in early childhood

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Cystic fibrosis is a genetic disorder without a cure, but triple therapy treatment since 2020 has targeted its root cause. New research shows that this triple therapy is highly effective in children aged 2 to 11, restoring near-normal function of molecular channels in mucous membranes.

Cystic fibrosis is an incurable genetic disorder. Since 2020, a treatment known as triple therapy has addressed the underlying cause. Researchers at Charité – Universitätsmedizin Berlin found that the therapy is particularly effective in early childhood: Molecular channels in the mucous membranes, which do not function or function poorly in people with cystic fibrosis, reached nearly normal functional levels in children ages 2 to 11 following treatment.